Long-Term Therapeutic Efficacy of Intravenous AAV-Mediated Hamartin Replacement in Mouse Model of Tuberous Sclerosis Type 1

Document Details

Document Type
Pub Defense Publication
Publication Date
Dec 01, 2019
Source ID
10.1016/j.omtm.2019.08.003

Entities

People

  • Anat Stemmer-Rachamimov
  • Bakhos A Tannous
  • Casey A Maguire
  • David J Kwiatkowski
  • Eloise Hudry
  • Maria Gianatasio
  • Max Zinter
  • Miguel Sena-esteves
  • Pike See Cheah
  • Roderick T. Bronson
  • Shilpa Prabhakar
  • Xandra O. Breakefield
  • Xuan Zhang

Organizations

  • National Institutes of Health
  • United States Department of Defense