Targeting RyR Activity Boosts Antisense Exon 44 and 45 Skipping in Human DMD Skeletal or Cardiac Muscle Culture Models

Document Details

Document Type
Pub Defense Publication
Publication Date
Dec 01, 2019
Source ID
10.1016/j.omtn.2019.09.020

Entities

People

  • Christopher Hsu
  • Emilie D. Douine
  • Eugene E. Marcantonio
  • Florian Barthélémy
  • M. Carrie Miceli
  • Richard T Wang
  • Stanley F. Nelson

Organizations

  • California Institute for Regenerative Medicine
  • United States Department of Defense