The individual (single patient) IND for inborn errors of metabolism

Document Details

Document Type
Pub Defense Publication
Publication Date
Sep 01, 2015
Source ID
10.1016/j.ymgme.2014.10.003

Entities

People

  • Jakub Tolar
  • Patricia I. Dickson

Organizations

  • BioMarin Pharmaceutical
  • DEBRA
  • National Center for Advancing Translational Sciences
  • National Institute of Neurological Disorders and Stroke
  • National Institutes of Health
  • Shire (Ireland)
  • United States Department of Defense