Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy
Document Details
- Document Type
- Pub Defense Publication
- Publication Date
- Nov 01, 2021
- Source ID
- 10.1016/j.ymthe.2021.09.003
Entities
People
- Adrian Pickar‐Oliver
- Aravind Asokan
- Charles A. Gersbach
- Garth Devlin
- Heather Daniels
- Jacqueline N. Robinson-hamm
- Joel D. Bohning
- Siyan Liu
- Veronica Gough
- William H Majoros
Organizations
- National Institutes of Health