Optimization of the Linker Domain in a Dimeric Compound that Degrades an r(CUG) Repeat Expansion in Cells

Document Details

Document Type
Pub Defense Publication
Publication Date
Jul 13, 2020
Source ID
10.1021/acs.jmedchem.0c00558

Entities

People

  • Alicia J. Angelbello
  • Masahito Abe
  • Matthew D Disney
  • Raphael I. Benhamou
  • Samantha M. Meyer
  • Shruti Choudhary

Organizations

  • Muscular Dystrophy Association
  • Myotonic Dystrophy Foundation
  • National Ataxia Foundation
  • National Institute of Neurological Disorders and Stroke
  • Scripps Research
  • United States Department of Defense