Neurosteroids reverse tonic inhibitory deficits in Fragile X syndrome mouse model

Abstract

Fragile X syndrome (FXS) is the most common form of inherited intellectual disability. In addition, there is increased incidence of anxiety, sleep irregularities, and seizure activity. The underlying cause of FXS is a loss of the fragile X mental retardation protein (FMRP) which has been shown to participate in the biosynthesis of δ subunits. Studies from both FXS patients and animal models have revealed reduced expression levels of GABAAR α4 and δ subunits with a reduced efficacy of tonic inhibition. Neurosteroids (NS) are known allosteric modulators of GABAAR channel function but recent studies from our laboratory have revealed that NS also exert persistent effects on the efficacy of tonic inhibition by increasing the PKC‐mediated phosphorylation of the α4 subunit which increases the membrane expression and boosts tonic inhibition. We have used a combination of biochemical and electrophysiological methods to assess alterations in GABAergic signaling in the hippocampus of FMRP knock‐out mouse (Fmr1 KO), a widely validated model of the human syndrome.

Document Details

Document Type
Pub Defense Publication
Publication Date
Apr 01, 2017
Source ID
10.1096/fasebj.31.1_supplement.815.12

Entities

People

  • Amit A Modgil
  • James Doherty
  • Manasa Parakala
  • Mike Ackley
  • Paul A. Davies
  • Stephen J. Moss

Organizations

  • Simons Foundation
  • Tufts University
  • United States Department of Defense

Tags

Fields of Study

  • Biology

Readers

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