Poly(GP) proteins are a useful pharmacodynamic marker for C9ORF72 -associated amyotrophic lateral sclerosis
Abstract
Poly(GP) proteins are a promising pharmacodynamic marker for developing and testing therapeutics for treating C9ORF72 -associated amyotrophic lateral sclerosis.
Document Details
- Document Type
- Pub Defense Publication
- Publication Date
- Mar 29, 2017
- Source ID
- 10.1126/scitranslmed.aai7866
Entities
People
- Abhishek Datta
- Adam L. Boxer
- Alessandro Prelle
- Alexander Mccampbell
- Aliesha Garrett
- Amelia Robertson
- Ana M. Caputo
- Antonia Ratti
- Barbara Poletti
- Beth K. Rush
- Bruce L. Miller
- Bryan J. Traynor
- Carla Palmucci
- Casey Cook
- Chris W. Lee
- Christina N. Fournier
- Christine Ambrose
- Cinzia Tiloca
- Claudia Morelli
- David Lacomis
- Denitza Raitcheva
- Dennis W. Dickson
- Edythe Wiggs
- Emilie A. Perkerson
- Federica Solca
- Frank Rigo
- Giovanna Antognetti
- James D. Berry
- Jeannette N. Stankowski
- Jeannie Chew
- Jeffrey D Rothstein
- Jennifer D. Mcbride
- Jennifer Farren
- Jennifer Jockel-Balsarotti
- Jimei Tong
- Joanne Wuu
- John C. Van Swieten
- John D. Fryer
- John Q. Trojanowski
- Jon B. Toledo
- Jonathan D. Glass
- Karen Jansen-West
- Kevin B. Boylan
- Laura Braun
- Lauren B. Elman
- Leo F. Mccluskey
- Leonard Petrucelli
- Lilia J. Tabassian
- Lillian M. Daughrity
- Linda Rousseau
- Lindsey R. Hayes
- Luc Pregent
- Marka van Blitterswijk
- Mary Kay Floeter
- Matthew D Disney
- Mei Yue
- Mercedes Prudencio
- Michael Benatar
- Michael G. Heckman
- Michael Tierney
- Monica Castanedes-Casey
- Murray Grossman
- Nancy N. Diehl
- Otto Pedraza
- Pamela Desaro
- Robert Bowser
- Robert H. Brown
- Rosa Rademakers
- Shafeeq S Ladha
- Tania F. Gendron
- Timothy M Miller
- Veronique Belzil
- Vincenzo Silani
- Virginia Phillips
- Weixing Yang
- William T. Hu
- Yari Carlomagno
- Yong-Jie Zhang
- Yuping Song
Organizations
- ALS Association
- ALS Therapy Alliance
- Barrow Neurological Institute
- Biogen
- Emory University
- Erasmus MC
- Ionis Pharmaceuticals
- Johns Hopkins University
- Massachusetts General Hospital
- Mayo Clinic
- Mayo Clinic Graduate School of Biomedical Sciences
- Muscular Dystrophy Association
- National Institute of Neurological Disorders and Stroke
- National Institute on Aging
- Scripps Research
- United States Department of Defense
- University of California, San Francisco
- University of Miami
- University of Milan
- University of Pennsylvania
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- Washington University in St. Louis