AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice
Document Details
- Document Type
- Pub Defense Publication
- Publication Date
- Dec 06, 2018
- Source ID
- 10.1172/jci.insight.124297
Entities
People
- Aihua Dai
- Chady H. Hakim
- Charles A. Gersbach
- Christopher E Nelson
- Dongsheng Duan
- Gregory J Jenkins
- Jacqueline A. Louderman
- Kasun Kodippili
- Keqing Zhang
- Lakmini P. Wasala
- Michael E. Nance
- N. Nora Yang
- Nalinda B. Wasala
- Shi-Jie Chen
- Thais B. Lessa
- Xiufang Pan
- Yongping Yue
Organizations
- Muscular Dystrophy Association
- National Institutes of Health
- United States Department of Defense