Toward Novel Therapeutics for TSC and LAM: Using Mechanisms of a Bacterial Protein to Sensitize Cells to Rapamycin

Abstract

This project is based on our discovery that a bacterial protein (Shigella OspB) sensitizes mammalian cells to rapamycin-mediated inhibition of mTORC1 and that this mechanism of sensitizing cells to rapamycin appears to be conserved across divergent branches of life. The most significant finding of the current funding period is that the arginine N-end rule pathway and the inositol phosphate hexakisphosphate are required for OspB function. We isolated or generated anew, and confirmed, Saccharomyces cerevisiae strains with deletions in each of the genes that encode the first three steps of the arginine N-end rule pathway (nta1, ate1, and rad6), in the gene that encodes the enzyme that synthesizes hexakisphosphate (ipk1), and in genes that encode the enzyme that convert hexakisphosphate to pyrophosphate molecules (vip1 and ksc1). We found that each of the genes that encode the first three steps of the arginine N-end rule pathway and ipk1 are required for OspB function, but that vip1 and ksc1 are not. In follow-up to these results, we will test the role of these pathways in the function of OspB in mammalian cells. These findings provide new insight into OspB function.

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Document Details

Document Type
Technical Report
Publication Date
Jul 01, 2018
Accession Number
AD1063028

Entities

People

  • Marcia B Goldberg

Organizations

  • Massachusetts General Hospital

Tags

DTIC Thesaurus Topics

  • Amino Acids
  • Bacterial Proteins
  • Biomedical Research
  • Caffeine
  • Cells
  • Chemical Compounds
  • Chemical Synthesis
  • Chemistry
  • Cysteine
  • Degradation
  • Health Services
  • Identification
  • Inhibition
  • Mass Spectrometry
  • Medical Personnel
  • Molecules
  • Phenotypes
  • Proteins
  • Recognition
  • Spectrometry
  • Substrates
  • Sugar Alcohols
  • Sugar Phosphates
  • Therapy

Fields of Study

  • Biology

Readers

  • Aquatic Ecology
  • Molecular Biology and Genetics