Forward Genetic Screen to Identify Novel Therapeutic Entry Points of an Autism Spectrum Disorder

Abstract

During the reporting period, the PCR libraries from the primary screen were sequenced. The sequencing data sets then underwent quality control. Bioinformatics of the sequencing data identified those genes with significantly increased abundance of EGFP:Shank3. The positive hits from the kinase/phosphatase sub-library were then tested in a secondary screen with siRNA depletion of those hits and measurement of EGFP:Shank3 abundance by flow cytometry. The two most robustly increased gene from the kinase/phosphatase sub-library are now undergoing validation by Western blotting. These same two candidate hits will be tested for Shank3 protein regulation by knockdown in primary mouse neurons. We have already discovered that the protein complex for one of these hits interacts with Shank3 in vivo.

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Document Details

Document Type
Technical Report
Publication Date
Aug 01, 2019
Accession Number
AD1094712

Entities

People

  • Jimmy Jr L. Holder

Organizations

  • Baylor College of Medicine

Tags

Communities of Interest

  • Biomedical

DTIC Thesaurus Topics

  • Autism
  • Biomedical Information Systems
  • Biomedical Research
  • Cell Line
  • Cells
  • Computational Biology
  • Diseases And Disorders
  • Factor Analysis
  • Kinases
  • Medical Personnel
  • Proteins
  • Quality Control
  • Small Molecules
  • Spectra
  • Statistical Analysis
  • Stem Cells
  • Validation

Fields of Study

  • Biology

Readers

  • Child and Adolescent Substance Abuse Science in Autism Spectrum Disorders.
  • Molecular Genetics

Technology Areas

  • Biotechnology