Transcriptional Regulation and Targeting of NF1 Gene Expression

Abstract

An essential requirement in understanding how genes contribute to genetic disease is the thorough knowledge of the mechanisms controlling gene expression at the level of transcription. In this project we are identifying and functionally characterizing the NF1 regulatory region, and evaluating the molecular mechanisms that regulate NF1 transcription during normal cellular differentiation and the events leading to NF1 -related neoplasia. Overlapping regions of the NFl proximal promoter have been cloned using a series of DNA fragments created by PCR and characterized for use in the luciferase assays to isolate specific binding motifs near the NF1 transcription start site. Luciferase reporter assays have identified a 425 bp region displaying activities 50 to 80 higher than baseline reporter levels. Mutations at putative CRE and SP1 binding sites immediately 5' to the transcription start site have dramatic effects that lead to a 70-90% decrease in reporter activity. As well, these assays have revealed a putative repressor region within the NFl promoter region corresponding to CCCTC rich sequences between the transcription and translation start sites. Preliminary gelshift assays confirm binding of SP1 and CRE to their putative recognition sequences and provide the first evidence identifying functional sites likely involved in regulating NF1 transcription.

Open PDF

Document Details

Document Type
Technical Report
Publication Date
Oct 01, 2001
Accession Number
ADA407208

Entities

People

  • David I. Rodenhiser

Tags

DTIC Thesaurus Topics

  • Cell Line
  • Cells
  • Corrosion Resistant Steels
  • Diseases And Disorders
  • Gene Expression
  • Genetic Phenomena
  • Genetics
  • Health Services
  • Identification
  • Mutations
  • Neoplasms
  • Neuromuscular Diseases
  • Proteins
  • Recognition
  • Regulations
  • Sequences
  • Targeting

Fields of Study

  • Biology

Readers

  • Molecular Genetics
  • Molecular and genetic basis of cancer.

Technology Areas

  • Biotechnology