Development of Genetic Therapies for the Hemidesmosol Subtypes of Junction Epidermolysis Bullosa

Abstract

During the final award period of this project, we focused on creating the model systems for the in vitro gene therapy experiments, in particular, the in vitro skin model. We worked extensively on development of the in vitro skin model, and succeeded in generating recombinant skin between keratinocytes and dermal cells in skin equivalents. To extend these studies and make them more widely applicable for wound care enhancement in blistering diseases as well as in chemically induced wounding, we then went on to develop a model for in vitro epithelial reprogramming, in which we have begun to utilize different epithelial cell types as donor cells, in addition to keratinocytes, specifically, amnion and cornea cells. Collectively, we have shown that the use of gene delivery combined with epithelial cell-skin equivalent models, show significant promise toward developing a cellular 'bandage' for both genetically and chemically induced skin blistering.

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Document Details

Document Type
Technical Report
Publication Date
Nov 01, 2003
Accession Number
ADA420130

Entities

People

  • Angela M. Christiano

Organizations

  • Columbia University

Tags

DTIC Thesaurus Topics

  • Cells
  • Connective Tissue
  • Gene Therapy
  • Genetics
  • Health Services
  • Medical Personnel
  • Skin Diseases

Fields of Study

  • Biology

Readers

  • Molecular and Cellular Biochemistry
  • Molecular and Cellular Biology
  • Neurotrauma and Rehabilitation Medicine.

Technology Areas

  • Biotechnology