Identification of the Gene for Scleroderma in the Tsk/2 Mouse Strain: Implications for Human Scleroderma Pathogenesis and Subset Distinctions

Abstract

This project is focused on an animal model of the human disease, systemic sclerosis (SSc), called Tsk2/+. The SSc-like traits in Tsk2/+ heterozygotes are highly penetrant. With their readily apparent skin fibrosis resulting from ECM anomalies, Tsk2/+ mice have signs that resemble human SSc features, making it useful as a pre-clinical model. In this report, we show a clear time dependence on the gene expression in the skin of the Tsk2/+ mice. We have pinpointed a mutation in Col3a1 that is the Tsk2 gene, and have confirmed the sequence difference between Tsk2/+ and the parent strain, 101/H. We present results on the expression of TGFbeta mRNA from cells cultured from Tsk2/+ and WT littermates that suggest a mechanism for the up-regulation of TGFbeta seen in the mutant strain. We show that elastin content in the skin, known to be controlled by TGFbeta and possibly up-egulated in SSc, is the earliest indicator of tight-skin in the tissue. Finally, we show that Tsk2/+ mice, and mouse fibroblasts transfected with Col3a1 from Tsk2/+, share a substantial fibrotic gene expression program compared to WT mice or transfectants, indicating that expression of the Col3a1Tsk2 gene alone accounts for the trait in Tsk2/+ mice.

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Document Details

Document Type
Technical Report
Publication Date
Sep 01, 2014
Accession Number
ADA613448

Entities

People

  • Carol Artlett
  • Elizabeth P. Blankenhorn
  • Michael Whitfield

Organizations

  • Drexel University

Tags

Communities of Interest

  • Biomedical

DTIC Thesaurus Topics

  • Biological Factors
  • Cells
  • Chemical Synthesis
  • Chemistry
  • Connective Tissue Diseases
  • Genetics
  • Health Services
  • Hepatitis
  • Lung Diseases
  • Peptide Growth Factors
  • Peptides
  • Proteins
  • Skin Diseases

Fields of Study

  • Biology

Readers

  • Exercise and Sports Science.
  • Immunology and Pathology
  • Molecular Genetics